May. 15 at 10:34 AM
$SRPT So Rgnx did not reach 10% d production in some kids, Elevidys averaged over 60% in all kids more the 140. In embark the younger age group 4-5 was strongly state sig on NSAA, the 6- 7 just missed( some were stat sig some were not). Sarepta trialed more then 125, and treated in commercial setting more then 1000 Safely with few ALI's, to say RNNX drug is safe is premature. after treating only 30 kids. More importantly Elevidys every kid trialed remained above baseline in timed tests and NSAA thru 3, 4, 5 years. the Original 4 kids are still there after nearly 6 years. RGNX drug has a long way to go and a long time to get there before any kid see's it commercially if ever. They are in piss poor financial shape and dang well could go broke. My guess is they will drop the drug. JMO
