Oct. 24 at 7:16 PM
$LRMR
LRMR 's drug will likely be priced from $ 800K - one mil per year. IMHO.
Look at other rare disease like DMD drugs, it costs about
$700 - one mil a year.
but FA is more rare than DMD, and LRMR's drug is treating the root of FA, most DMD drugs just treat some symptoms of DMD.
In US, there are about 5,000 FA patients while DMD has about 15,000 patients.
The price of the drug is proportional to the rare-ness of the disease.
An example: this is recently approved drug for DMD:
