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Market Cap 3B P/E - EPS this Y 23.80% Ern Qtrly Grth -
Income -585.12M Forward P/E -6.64 EPS next Y 18.10% 50D Avg Chg -10.00%
Sales 481.3M PEG -0.23 EPS past 5Y - 200D Avg Chg -2.00%
Dividend N/A Price/Book 13.57 EPS next 5Y 37.90% 52W High Chg -25.00%
Recommedations 1.70 Quick Ratio 3.20 Shares Outstanding 92.17M 52W Low Chg 27.00%
Insider Own 3.64% ROA -23.42% Shares Float 88.85M Beta 0.57
Inst Own 99.08% ROE -208.43% Shares Shorted/Prior 3.61M/3.85M Price 42.35
Gross Margin -49.52% Profit Margin -121.57% Avg. Volume 596,267 Target Price 89.80
Oper. Margin -79.14% Earnings Date Oct 31 Volume 434,266 Change -1.33%
About Ultragenyx Pharmaceutical Inc.

Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX111, an AAV9 gene therapy product candidate for the treatment of patients with Sanfilippo syndrome type A, or MPS IIIA, a rare lysosomal storage disease; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc.; Solid Biosciences Inc.; Regeneron; Abeona; and Daiichi Sankyo Co., Ltd. The company was incorporated in 2010 and is headquartered in Novato, California.

Ultragenyx Pharmaceutical Inc. News
11/20/24 Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)
11/09/24 Ultragenyx Presents Positive Update on GTX-102 Angelman Syndrome Program at FAST’s 17th Annual Global Science Summit
11/07/24 Ultragenyx Pharmaceutical Third Quarter 2024 Earnings: Beats Expectations
11/06/24 Ultragenyx Q3 Loss Narrower Than Expected, Revenues Beat Estimates
11/06/24 Ultragenyx Pharmaceutical Inc (RARE) Q3 2024 Earnings Call Highlights: Robust Revenue Growth ...
11/05/24 Ultragenyx: Q3 Earnings Snapshot
11/05/24 Ultragenyx Reports Third Quarter 2024 Financial Results and Corporate Update
11/01/24 What Makes Ultragenyx Pharmaceutical (RARE) an Exciting Investment Opportunity?
10/29/24 Ultragenyx to Host Conference Call for Third Quarter 2024 Financial Results and Corporate Update
10/23/24 Recent 4.1% pullback isn't enough to hurt long-term Ultragenyx Pharmaceutical (NASDAQ:RARE) shareholders, they're still up 70% over 1 year
10/08/24 RARE's Bone Disorder Drug Gets FDA's Breakthrough Therapy Tag
10/07/24 Ultragenyx Receives Breakthrough Therapy Designation for Setrusumab (UX143) in Osteogenesis Imperfecta
10/04/24 RARE's Wilson Disease Candidate Betters Standard Therapy in Study
10/03/24 Ultragenyx Provides Update on Stage 1 Cohorts in Pivotal Phase 1/2/3 Cyprus2+ Study Evaluating UX701 Gene Therapy for the Treatment of Wilson Disease
09/26/24 Ultragenyx Announces Upcoming Setrusumab (UX143) Presentations at the ASBMR 2024 Annual Meeting
09/05/24 Ultragenyx Pharmaceutical Inc. (RARE): Among the Best Mid-Cap Healthcare Stocks To Buy Now
08/29/24 Ultragenyx to Participate in Investor Conferences in September
08/06/24 3 Genomics Stocks That May Transform Personalized Medicine
08/02/24 Ultragenyx (RARE) Q2 Loss Narrower Than Expected, Revenues Up
08/01/24 Ultragenyx: Q2 Earnings Snapshot
RARE Chatroom

User Image BottomFishingCharts Posted - 10 hours ago

#Bitcoin is chewing through $97K atm and momentum is just starting to pivot which bodes well for a 100K #BreakOut.. #LetsGo #Altcoins.. $RARE @SuperRare / $BONK @bonk_inu / $SWFTC @SwftCoin / $MOBILE @helium_mobile @heliumFndn $BTC / $BTC.X

User Image JimiJoJeeter Posted - 23 hours ago

$ABEO With $RARE BLA news on deck b4 EOY, I'm surprised we're not higher; but, it's a good entry point...

User Image CrispDry Posted - 23 hours ago

$MREO $RARE rare is winning between the two

User Image Elvira007 Posted - 2 days ago

$MREO No one and I mean NO ONE wants to see CEO DSK trying to launch Setrusumab for OI in Europe even if its an easy drug to launch with a small sales force. Just give it to $RARE, they already have the salesforce and contacts in place. Why train a new team and screw your partners over. Let them have it, take a 20% royalty (with a big upfront)...Its that fucking easy. Partner out AATD or sell it outright and then go back to looking for new assets to develop and partner again to big pharma....It worked for Ligand. Stock was $10. peaked at $270....They had 20 employees at the time

User Image LDT79 Posted - 2 days ago

@grod86 my guess is they will go solo with $RARE 's milestone payment

User Image CrispDry Posted - 2 days ago

$MREO sold like 80% of my holding and rolled into $RARE

User Image Sergecker Posted - 5 days ago

$BHVN $RARE 😏🚀 MYNZ We know the date of the reverse split (RS) if there will be one, but possibly a Nasdaq extension will be granted. Last time it traded, 50 million and 19 million heavy shorts attacked. Now, it has huge credibility after the TMO partnership and the meeting. The company will decide by November 25th whether or not to do an RS based on Nasdaq's response. Anyway, after the RS, I'm not worried about what happens next. A $210 billion partner TMO signing a deal with a penny stock has never happened before. I will be loading heavy on Monday. This will go to the moon like the DRUG stock recently did. The price target (PT) is $50. The squeeze will be parabolic.

User Image swingingtech Posted - 1 week ago

$RARE https://wallstreetwaves.com/rare-hits-significant-low-crossing-below-key-moving-average/

User Image LDT79 Posted - 1 week ago

@HillbillyWilly @stockythebull she will not release any news whatsoever - Alvelestat will end up like TIGIT - this company's only hope is $RARE with Setrusumab - CEO is completely useless if not detrimental for the stock and company - Rubric is the laziest activist !

User Image BottomFishingCharts Posted - 1 week ago

$RARE .. @SuperRare

User Image BottomFishingCharts Posted - 1 week ago

#AltCoins like $BONK (@bonk_inu), $RARE (@SuperRare) and $JASMY (@JasmyMGT) are starting to #BreakOut and p/u steam... #LetsGo #Bitcoin, $BTC / $BTC.X... #KeepItGoing

User Image RonIsWrong Posted - 1 week ago

$RARE Ultragenyx Presents Positive Update on GTX-102 Angelman Syndrome Program at FAST’s 17th Annual Global Science Summit Phase 1/2 data show improvements across all domains and confirm that Phase 3 Aspire study is amply powered to establish efficacy of GTX-102 Phase 3 program on track to begin enrollment by end-of-year

User Image Stocksrunner Posted - 1 week ago

🔥 Weekend Markets Tea: Just spilled all the hot stock gossip! $PLTR stealing the AI spotlight (again!), $SHW getting that blue-chip glow-up joining the Dow, $RARE crushing it with clinical data, Full tea here https://stocksrunner.com/posts/1355

User Image abubnic Posted - 2 weeks ago

$RARE Q3: 42% increase in income, led by the performance of Crysvita, a treatment for a form of rickets, a bone disease. This drug listed among Ultragenyx’s product line brought in $97.84M for the past three months — about $23M vs the same period last year. https://ir.ultragenyx.com/news-releases/news-release-details/ultragenyx-reports-third-quarter-2024-financial-results-and

User Image 360sage Posted - 2 weeks ago

$RARE This is a potential 2-3X opportunity. They are growing, and have a strong pipeline

User Image OutperformGER Posted - 2 weeks ago

$MREO and $RARE for Setrusumab 👇

User Image haitbaslam Posted - 2 weeks ago

$RARE Ultragenyx Pharmaceutical Inc. reported its financial results for the third quarter of 2024 on November 5, after the close of the U.S. markets. Key takeaways include: Financial Performance: Total Revenue: The company reported total revenue of $147 million for the third quarter of 2024, an increase of 36% over the same period in 2023. Crysvita®: Crysvita revenue was $114 million, representing growth of 37% over the third quarter of 2023. The increase was primarily driven by increased international demand. Dojolvi®: Dojolvi revenue was $19 million, up 17% from the prior year. Evkeeza®: Evkeeza revenues reached $8 million, reflecting growing demand in the Company’s territories outside the United States. 2024 Outlook: Ultragenyx raised its full-year 2024 revenue guidance to $530 million to $550 million, compared to its previous estimate of $500 million to $530 million.

User Image DonCorleone77 Posted - 2 weeks ago

$RARE Ultragenyx backs FY24 revenue view $530M-$550M, consensus $536.8M The company said, "Crysvita revenue to be towards the upper end of the range of $375 million to $400 million. This includes all regions where Ultragenyx will recognize revenue: product sales in Latin America and Turkey, royalties in Europe, which have been ongoing, and royalties in North America, which began in April 2023. Dojolvi revenue to be in the range of $75 million to $80 million Net Cash Used in Operations of around $400 million."

User Image DonCorleone77 Posted - 2 weeks ago

$RARE Ultragenyx reports Q3 EPS ($1.40), consensus ($1.45) Reports Q3 revenue $139.49M, consensus $135.79M. "We continue to see substantial year-over-year revenue growth from our commercial portfolio as we expand geographic access to our medicines. This growth could accelerate with up to three near-term BLA submissions and approvals," said Emil Kakkis, chief executive officer and president of Ultragenyx. "Today, we are also sharing an important update from our Phase 3 study in GSDIa with substantially larger reductions in cornstarch intake in crossover patients treated with DTX401. As in our Phase 2 patients, we observed that patients and their physicians were far more comfortable with aggressive titration of cornstarch once they were confirmed to be treated with the gene therapy and had direct access to timely glucose readings."

User Image RonIsWrong Posted - 2 weeks ago

$RARE Ultragenyx Reports Third Quarter 2024 Financial Results and Corporate Update --- Third quarter 2024 total revenue grew 42% versus prior year to $139 million, including Crysvita® revenue of $98 million and Dojolvi® revenue of $21 million Reaffirmed 2024 expected total revenue guidance of $530 million to $550 million Breakthrough Designation granted for setrusumab (UX143) in osteogenesis imperfecta DTX401 Phase 3 follow-up data demonstrated higher and faster 62% mean reduction in cornstarch in crossover patients with glycogen storage disease type Ia (GSDIa)

User Image Estimize Posted - 2 weeks ago

$RARE reports after the close, Estimize Consensus +0.06 EPS and +3.04M Revs compared to WS http://www.estimize.com/rare/fq3-2024?utm_conten

User Image Elvira007 Posted - 2 weeks ago

@Jcody1966 HOLD. Despite CEO being a total fucking LIAR, you have to rely on Ultragenyx and their CEO who is one of the best. He will get Setrusumab across the finish line... Likely, it makes sense for $RARE to acquire MREO. If not, stock still goes higher.....I think worth $15-$20 in a takeout on approval. In terms of their other drugs. No one knows WTF she is doing, especially Alvelestat.

User Image Nyomi__Holloway Posted - 2 weeks ago

$CORT $RARE MYNZ +10.91% PM LFG, unusually high volume activity last week, apx 30% more than average. 👇😘🚀 This stock may see the last time this price per share PT $5+ 🚀 HUGE PRs drop incoming before the Nov 13 meeting, so compliance is coming—no RS needed. Here is why… 1.Frankie Muniz backing Mainz (yes, the Malcolm guy & NASCAR #33 now repping MYNZ). 2.Petra, ex-Obama advisor, hinted at a big U.S. lab partner. Solid source! 3.Six news hits in 3 weeks—momentum. 4.Already solid in the EU, not new but expanding, with insurance covering their tests. 5.Their test has 88% accuracy vs. EXAS (42%) & GH (20%)—big edge! 6.$1.5M private placement in the bag. 7.CEO teased big plans ahead.

User Image ChessGM Posted - 2 weeks ago

$RARE Heads up alert! Only three days until Upcoming Earnings on Tuesday, 11/5/2024 Bullish (8.3) Ultragenyx Pharmaceutical Inc. (RARE) has shown strong momentum recently, particularly with the favorable reception of its investigational therapies. The company received Breakthrough Therapy Designation from the FDA for setrusumab, aimed at treating osteogenesis imperfecta, which positions it favorably within the competitive landscape of rare disease treatments. Additionally, the recent Phase 1/2/3 results for the UX701 gene therapy for Wilson disease indicated superior efficacy compared to standard therapies, suggesting a robust pipeline that could drive future revenue growth. Financially, Ultragenyx aims to leverage its promising clinical data to enhance its market valuation, with the current P/E ratio at 18.5, which is below the industry average of around 20. This suggests that the stock may be undervalued relative to its growth potential. Analysts forecast a 15% year-over-year growth in EPS, driven by anticipated approvals and market entry of its therapies. Revenue estimates for the upcoming quarters reflect optimism, with projections indicating potential growth from $250 million in 2024 to over $400 million by 2026, contingent on successful commercialization of its pipeline products. Regarding upcoming earnings, Ultragenyx is scheduled to report its third-quarter results on November 5, 2024. Analysts are closely watching this event, with consensus estimates suggesting a revenue of approximately $60 million, marking a 25% increase from the prior year. Historical performance during earnings announcements has shown a tendency to meet or exceed expectations, which could bolster investor confidence and drive stock price appreciation. Given the recent positive developments in its drug pipeline and the anticipated financial results, the outlook remains robust, with a potential positive impact on the stock following the earnings call. - Funds were net buyers of $RARE during the previous reporting quarter. - Top 5 funds with large holdings in $RARE: * Alkeon Capital Management LLC $92MM. CGMRank: 91% * Baker Brothers Advisors LP $60MM. CGMRank: 75% * Adage Capital P $46MM. CGMRank: 87% * Avoro Capital Advisors LLC $34MM. CGMRank: 85% * Mpm Bioimpact LLC $16MM. CGMRank: 52% - Last 10 days performance: -7% - Last 30 days performance: -8% - Last 90 days performance: 1% Negative price momentum. Follow ChessGM! Make your move and get timely earnings alerts from ChessGM. Not a financial advice.

User Image 360sage Posted - 10/30/24

$RARE Earnings are coming

User Image PDM5 Posted - 1 month ago

$MREO $RARE BofA... "Notably, the company is expecting to take two interim looks at the phase 3 Orbit study evaluating setrusumab in osteogenesis imperfecta (OI) to see if the study can be stopped early to support a bid for approval. The first interim is expected around year-end with the second coming several months after. Our base case continues to assume the study will need to reach at least the second interim so an earlier stop at the first interim would provide upside opportunity. We currently model a launch in 2026 (60% likelihood-of-success) and peak worldwide nominal sales of $1.7bn in 2035. We continue to highlight RARE as one of our top picks of 2024 given a catalyst rich pipeline in high unmet need rare disease indications and reiterate our Buy with $83 PO."

User Image insiderbuyingselling Posted - 1 month ago

$RARE new insider selling: 7465 shares. http://insiderbuyingselling.com/?t=RARE

User Image pc95035 Posted - 1 month ago

User Image LDT79 Posted - 1 month ago

$MREO and down we go again while $RARE is up 3% - the hate towards our CEO is real

User Image Westieofwallst Posted - 1 month ago

@LDT79 they have a PR on their website - identical to the $rare one.

Analyst Ratings
Cantor Fitzgerald Overweight Oct 1, 24
RBC Capital Outperform Sep 26, 24
Cantor Fitzgerald Overweight Sep 20, 24
Cantor Fitzgerald Overweight Sep 16, 24
Barclays Overweight Aug 5, 24
Wells Fargo Overweight Aug 2, 24
Goldman Sachs Buy Aug 2, 24
Cantor Fitzgerald Overweight Aug 2, 24
Wedbush Neutral Aug 2, 24
Insider Trades Relationship Date Transactions Cost($) #Shares Value($) #Share Own SEC Form 4
Kassberg Thomas Richard CBO & EVP CBO & EVP Oct 23 Sell 32.78 39,878 1,307,201 246,860 10/24/23
Kassberg Thomas Richard CBO & EVP CBO & EVP Oct 23 Option 6.86 39,878 273,563 286,738 10/24/23
KAKKIS EMIL D President & CEO President & CEO Oct 19 Sell 33.52 47,853 1,604,033 599,743 10/23/23
KAKKIS EMIL D President & CEO President & CEO Oct 19 Option 6.86 47,853 328,272 647,029 10/23/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Sep 07 Sell 39.67 2,163 85,806 23,614 09/11/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Sep 07 Option 21 2,000 42,000 25,777 09/11/23
Sanders Corazon (Corsee) D. Director Director Jun 30 Sell 46.76 585 27,355 8,985 06/30/23
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 19 Sell 48.20 305 14,701 57,281 06/21/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer May 09 Option 21.00 3,000 63,000 30,747 05/10/23
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 01 Sell 45.25 3,881 175,615 46,720 03/03/23
Parschauer Karah Herdman EVP and Chief Legal.. EVP and Chief Legal Officer Mar 01 Sell 45.25 3,161 143,035 56,139 03/03/23
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 01 Sell 45.27 1,968 89,091 250,254 03/03/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Mar 01 Sell 45.65 100 4,565 23,048 03/03/23
Huang Dennis Karl See Remarks See Remarks Mar 01 Sell 45.65 389 17,758 75,314 03/03/23
Pinion John Richard See Remarks See Remarks Mar 01 Sell 45.26 3,755 169,951 80,174 03/03/23
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Mar 01 Sell 45.25 3,664 165,796 57,344 03/03/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Dec 21 Sell 43.96 2,031 89,283 16,197 12/22/22
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Oct 14 Sell 40.16 1,629 65,421 66,695 10/17/22
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 19 Sell 54.78 295 16,160 36,160 06/22/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Apr 16 Sell 84.55 132 11,161 16,914 04/19/22
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 11 Sell 67.01 10,281 688,930 227,559 03/15/22
Parschauer Karah Herdman EVP and Chief Legal.. EVP and Chief Legal Officer Mar 07 Sell 62.95 5,140 323,563 34,438 03/08/22
Fust Matthew K Director Director Mar 04 Option 40.37 7,500 302,775 23,195 03/08/22
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Mar 01 Sell 65.59 954 62,573 51,808 03/03/22
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Mar 01 Sell 66.62 2,713 180,740 22,317 03/03/22
Pinion John Richard See Remarks See Remarks Mar 01 Sell 66.62 4,498 299,657 45,266 03/03/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Mar 01 Sell 66.62 843 56,161 13,229 03/03/22
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 01 Sell 66.62 2,821 187,935 33,938 03/03/22
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Jan 30 Sell 66.30 1,657 109,859 36,759 02/01/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Oct 14 Sell 81.14 140 11,360 14,072 10/18/21
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Oct 12 Sell 81.98 6,738 552,381 38,762 10/14/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Sep 09 Sell 100.65 7,336 738,368 28,668 09/09/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Sep 09 Option 54.5 7,336 399,812 36,004 09/09/21
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 23 Sell 94.8 1,009 95,653 25,708 06/23/21
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 03 Sell 138.17 4,572 631,713 107,181 03/03/21
Pinion John Richard See Remarks See Remarks Mar 03 Sell 138.17 6,198 856,378 50,237 03/03/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Mar 03 Sell 138.17 3,970 548,535 30,227 03/03/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Mar 03 Sell 138.17 732 101,140 16,544 03/03/21
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 03 Sell 138.18 4,543 627,752 39,139 03/03/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Jan 08 Option 21 4,000 84,000 20,436 01/08/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Jan 08 Sell 140.65 4,000 562,600 15,716 01/08/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 30 Option 54.5 97 5,286 24,065 10/30/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 30 Sell 100 97 9,700 23,968 10/30/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 13 Option 54.5 10,000 545,000 34,293 10/13/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 13 Sell 95 10,000 950,000 24,293 10/13/20