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Market Cap 3B P/E - EPS this Y 22.50% Ern Qtrly Grth -
Income -613.35M Forward P/E -6.64 EPS next Y 20.80% 50D Avg Chg -10.00%
Sales 442.59M PEG -0.76 EPS past 5Y - 200D Avg Chg -2.00%
Dividend N/A Price/Book 13.57 EPS next 5Y 8.90% 52W High Chg -25.00%
Recommedations 1.80 Quick Ratio - Shares Outstanding 83.13M 52W Low Chg 27.00%
Insider Own 4.03% ROA - Shares Float 72.27M Beta -
Inst Own 100.15% ROE - Shares Shorted/Prior 4.38M/3.78M Price 42.35
Gross Margin 71.75% Profit Margin -138.58% Avg. Volume 596,267 Target Price 89.30
Oper. Margin -151.93% Earnings Date Aug 1 Volume 434,266 Change -1.33%
About Ultragenyx Pharmaceutical Inc.

Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX111, an AAV9 gene therapy product candidate for the treatment of patients with Sanfilippo syndrome type A, or MPS IIIA, a rare lysosomal storage disease; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc.; Solid Biosciences Inc.; Regeneron; Abeona; and Daiichi Sankyo Co., Ltd. The company was incorporated in 2010 and is headquartered in Novato, California.

Ultragenyx Pharmaceutical Inc. News
02:01 PM Ultragenyx Pharmaceutical Inc (RARE) (Q1 2024) Earnings Call Transcript Highlights: Key ...
11:22 AM Ultragenyx (RARE) Q1 Loss Wider Than Expected, Revenues Rise Y/Y
05/02/24 Ultragenyx Pharmaceutical Inc (RARE) Q1 2024 Earnings: Misses EPS Estimates, Revenue Grows ...
05/02/24 Ultragenyx Reports First Quarter 2024 Financial Results and Corporate Update
04/30/24 Ultragenyx Issues 2023 Corporate Responsibility Report, Showcasing Commitment to Improving Equity and Access to Innovation in Rare Disease
04/30/24 Ultragenyx Announces Completion of Enrollment in Phase 3 Orbit and Cosmic Studies Evaluating Setrusumab (UX143) for the Treatment of Osteogenesis Imperfecta (OI)
04/25/24 Ultragenyx to Host Conference Call for First Quarter 2024 Financial Results and Corporate Update
04/19/24 Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)
04/16/24 Ultragenyx (RARE) Meets Efficacy Goal in Neuro Disease Study
04/15/24 Ultragenyx says Angelman therapy is working, but safety questions remain
04/15/24 Ultragenyx Announces Positive Interim Phase 1/2 Data in Patients with Angelman Syndrome After Treatment with GTX-102
04/12/24 Ultragenyx Announces Update to Conference Call Timing to Discuss New Data from GTX-102 in Patients with Angelman Syndrome
04/12/24 Ultragenyx Announces Upcoming Data Presentations at American Academy of Neurology (AAN) 2024 Annual Meeting
03/20/24 10 NASDAQ Stocks with Biggest Upside
03/12/24 Insider Sell: CBO & EVP Thomas Kassberg Sells 11,509 Shares of Ultragenyx Pharmaceutical ...
03/11/24 Director Matthew Fust Sells 12,195 Shares of Ultragenyx Pharmaceutical Inc (RARE)
03/08/24 10 Biotech Stocks with Huge Potential
02/27/24 Ultragenyx to Participate at Investor Conferences in March
02/17/24 Ultragenyx Pharmaceutical Full Year 2023 Earnings: Revenues Beat Expectations, EPS In Line
02/16/24 Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) Q4 2023 Earnings Call Transcript
RARE Chatroom

User Image insiderbuyingselling Posted - 5 hours ago

$RARE new insider selling: 354 shares. http://insiderbuyingselling.com/?t=RARE

User Image xbibackto70s Posted - 1 day ago

$RARE bios+ earnings=80% go down Fing sector sucks

User Image epsguid Posted - 1 day ago

$RARE reported a loss of $2.03, consensus was ($1.72) via @eWhispers #epsmiss http://eps.sh/d/rare

User Image Stock_Titan Posted - 1 day ago

$RARE Ultragenyx Reports First Quarter 2024 Financial Results and Corporate Update https://www.stocktitan.net/news/RARE/ultragenyx-reports-first-quarter-2024-financial-results-and-t5sjjtpnp1d9.html

User Image Quantumup Posted - 04/30/24

BTIG raised the PT on $MREO to $6 was $4/Buy + raised the probability of success (PoS) for setrusumab in Ol to 90% was 75%: 📝setrusumab reduced annualized fracture rate by 67% following 6mo Tx across 24 OI pts vs SoC bisphosphonate = 20% =g setrusumab to sig improve on SoC: $RARE

User Image Berakhot Posted - 04/30/24

$RARE $MREO

User Image Stock_Titan Posted - 04/30/24

$RARE Ultragenyx Issues 2023 Corporate Responsibility Report, Showcasing Commitment to Improving Equity and Access to Innovation in Rare Disease https://www.stocktitan.net/news/RARE/ultragenyx-issues-2023-corporate-responsibility-report-showcasing-wc1ktfbvtfuw.html

User Image OutperformGER Posted - 04/30/24

$MREO and $RARE 👇

User Image OutperformGER Posted - 04/30/24

$MREO and $RARE 👇

User Image briefingcom Posted - 04/30/24

$RARE: Ultragenyx Pharma announces that all patients have been enrolled across the Phase 3 Orbit and Cosmic studies evaluating setrusumab (UX143) in pediatric and young adult patients with osteogenesis imperfecta

User Image Elvira007 Posted - 04/30/24

$MREO $RARE already completed enrollment of its "recently" launched Orbit & cosmic Phase 3 studies and CEO is still talking about partnering Alveletstat for over 24 months. CEO needs to be removed once and for all......

User Image Stock_Titan Posted - 04/30/24

$RARE Ultragenyx Announces Completion of Enrollment in Phase 3 Orbit and Cosmic Studies Evaluating Setrusumab (UX143) for the Treatment of Osteogenesis Imperfecta (OI) https://www.stocktitan.net/news/RARE/ultragenyx-announces-completion-of-enrollment-in-phase-3-orbit-and-po3p9jctg5yl.html

User Image Stock_Titan Posted - 04/25/24

$RARE Ultragenyx to Host Conference Call for First Quarter 2024 Financial Results and Corporate Update https://www.stocktitan.net/news/RARE/ultragenyx-to-host-conference-call-for-first-quarter-2024-financial-bv0nd6bnjkhs.html

User Image Thestocktraderhubzee Posted - 04/24/24

$RARE TD Cowen Maintains Buy on Ultragenyx Pharmaceutical, Raises Price Target to $61

User Image Stocksrunner Posted - 04/23/24

🎉 Exciting Analyst Upgrades Today! $DDOG Datadog surges post-Wells Fargo's upgrade to Overweight. $QCOM Qualcomm gains momentum as Benchmark initiates coverage with a Buy rating. $EQR BMO Capital upgrades Equity Residential to Outperform from Market Perform. $RARE RBC Capital initiates coverage of Ultragenyx Pharmaceutical with an Outperform recommendation. $RHI Truist Securities raises outlook for Robert Half from Sell to Hold. Stay tuned for potential opportunities! https://stocksrunner.com/upgrades

User Image DonCorleone77 Posted - 04/22/24

$RARE Ultragenyx initiated with an Outperform at RBC Capital RBC Capital analyst Luca Issi initiated coverage of Ultragenyx Pharmaceutical with an Outperform rating and $77 price target. The company has a $500M base business growing 30% ann7ally, which "protects the downside," the analyst tells investors in a research note. The firm is "impressed" by the 67% reduction in bone fractures seen for osteogenesis imperfecta and thinks it can be a $1B opportunity for Ultragenyx. The Phase III is "likely to hit," contends RBC.

User Image erevnon Posted - 04/22/24

RBC Capital initiates coverage on Ultragenyx Pharmaceutical $RARE at Outperform rating and a price target of https://marketsblock.com/stock-upgrades-and-downgrades/

User Image lidopete Posted - 04/22/24

$RARE $MREO 04:50 Rec-Initiate Ultragenyx initiated with an Outperform at RBC Capital RBC Capital analyst Luca Issi initiated coverage of Ultragenyx Pharmaceutical with an Outperform rating and $77 price target. The company has a $500M base business growing 30% ann7ally, which "protects the downside," the analyst tells investors in a research note. The firm is "impressed" by the 67% reduction in bone fractures seen for osteogenesis imperfecta and thinks it can be a $1Billion opportunity for Ultragenyx. The Phase III is "likely to hit," contends RBC.

User Image insiderbuyingselling Posted - 04/19/24

$RARE new insider selling: 142 shares. http://insiderbuyingselling.com/?t=RARE

User Image Stock_Titan Posted - 04/19/24

$RARE Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4) https://www.stocktitan.net/news/RARE/ultragenyx-reports-inducement-grant-under-nasdaq-listing-rule-5635-c-mc9bf36of5qv.html

User Image Pianomemo Posted - 04/15/24

$RARE Guess they have no real endpoints which makes it hard to measure if it is a success like survival etc

User Image briefingcom Posted - 04/15/24

$RARE: Ultragenyx Pharma (-6.4%) announces new data from the Phase 1/2 study of GTX-102 for the treatment of Angelman syndrome https://www.briefing.com/in-depth-analysis/content/article?ArticleId=IN20240415070441RARE&utm_campaign=inplay&utm_medium=social&utm_source=st&utm_content=view_page

User Image TraderMK Posted - 04/15/24

$RARE reports positive results but the stock tanks? What am I missing?

User Image OpenOutcrier Posted - 04/15/24

$RARE (-7.4% pre) Ultragenyx Pharma (RARE) Reports Positive Interim Phase 1/2 Data with GTX-102 - SI https://ooc.bz/l/30338

User Image xbibackto70s Posted - 04/15/24

$XBI recap for Monday. No buyouts, shocking! Shit data by $rare, and massive fail by $mrns down 70%+. And zero positive news today by biotech. Short this to the ground! It’s garbage!

User Image basscat12 Posted - 04/15/24

$RARE $MOH $SNBR $CRM Pre-Market Gap Down, delayed, courtesy barchart, presented here for @Vegas1 to help us follow the money!

User Image Maverick11 Posted - 04/15/24

$VKTX Fully fully loaded here w/ addition of May 80 calls on Friday. Added $RARE to this AM ahead of conference call - nonsensical action there. Fantastic opportunity. Continue to add $ALCC - AI name (energy) led by Sam Altman.

User Image briefingcom Posted - 04/15/24

Gapping down: $MRNS -74.2% $NMRA -13.7% $RARE -10.4% $CRM -2.6%

User Image OutperformGER Posted - 04/15/24

$RARE @USMA67Korea 👇

User Image DonCorleone77 Posted - 04/15/24

$RARE Ultragenyx announces results from interim Phase 1/2 data of GTX-102 Ultragenyx Pharmaceutical announced new data from the Phase 1/2 study of GTX-102 for the treatment of Angelman syndrome. Expansion Cohorts at Day 170: Cognition assessed by Bayley-4 showed rapid and clinically significant improvement compared with Natural History data. Day 170 data were consistent with the treatment benefit observed in the Dose-escalation Cohorts at a similar timepoint. Behavior assessed by the Angelman Severity Assessment showed rapid improvement exceeding the treatment benefit observed in the Dose-escalation Cohorts at Day 170. Hyperactivity and noncompliance assessed by the Aberrant Behavior Checklist-Community showed rapid and clinically significant improvement at Day 170 compared with Natural History data, providing further insight into one of the most commonly reported behavioral issues. Sleep assessed by ASA showed rapid and clinically meaningful improvement exceeding treatment benefit observed in the Dose-escalation Cohorts at Day 170. Receptive communication assessed by Bayley-4 showed rapid improvement compared with Natural History data. Day 170 data were consistent with the treatment benefit observed in the Dose-escalation Cohorts at a similar timepoint. Gross Motor function assessed by ASA showed rapid improvement exceeding the treatment benefit observed in the Dose-escalation Cohorts at Day 170. Gross motor assessments as measured by Bayley-4 were not performed at Day 170 in the Expansion Cohorts to reduce patient testing burden and are not included in this analysis at this timepoint. Multi-domain Responder Index analysis across the four domains of Cognition, Receptive Communication, Behavior and Sleep resulted in a total net response of +2.0. The majority of patients had already achieved a total net response of +2 to +4 domains, demonstrating improvement exceeding the minimally important difference threshold in several domains even at this early Day 170 timepoint. Dose-escalation Cohorts up to Day 758: Cognition assessed by Bayley-4 showed continuing long-term improvement compared with Natural History data and exceeded the threshold of clinical significance by many-fold in many patients. Behavior assessed by ASA showed continuing clinically meaningful improvement. Sleep assessed by ASA showed sustained clinically meaningful improvement. Receptive communication measured by Bayley-4 showed sustained and clinically significant improvement compared with Natural History data. Gross motor function assessed by Bayley-4 showed continued and clinically significant improvement compared with previously reported Natural History data. MDRI analysis across the four domains of Cognition, Receptive Communication, Behavior and Sleep resulted in a total net response of +2.0 (p-value = 0.0007) at Day 338. The majority of patients had a total net response of +2 to +4, as well as a 2- to 5-fold improvement over the MID threshold in several domains.

Analyst Ratings
Cantor Fitzgerald Overweight May 3, 24
Wedbush Neutral May 3, 24
TD Cowen Buy Apr 24, 24
RBC Capital Outperform Apr 22, 24
Wedbush Neutral Apr 17, 24
Wedbush Neutral Apr 16, 24
Cantor Fitzgerald Overweight Apr 5, 24
JP Morgan Overweight Mar 18, 24
JP Morgan Overweight Feb 27, 24
Insider Trades Relationship Date Transactions Cost($) #Shares Value($) #Share Own SEC Form 4
Kassberg Thomas Richard CBO & EVP CBO & EVP Oct 23 Sell 32.78 39,878 1,307,201 246,860 10/24/23
Kassberg Thomas Richard CBO & EVP CBO & EVP Oct 23 Option 6.86 39,878 273,563 286,738 10/24/23
KAKKIS EMIL D President & CEO President & CEO Oct 19 Sell 33.52 47,853 1,604,033 599,743 10/23/23
KAKKIS EMIL D President & CEO President & CEO Oct 19 Option 6.86 47,853 328,272 647,029 10/23/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Sep 07 Sell 39.67 2,163 85,806 23,614 09/11/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Sep 07 Option 21 2,000 42,000 25,777 09/11/23
Sanders Corazon (Corsee) D. Director Director Jun 30 Sell 46.76 585 27,355 8,985 06/30/23
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 19 Sell 48.20 305 14,701 57,281 06/21/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer May 09 Option 21.00 3,000 63,000 30,747 05/10/23
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 01 Sell 45.25 3,881 175,615 46,720 03/03/23
Parschauer Karah Herdman EVP and Chief Legal.. EVP and Chief Legal Officer Mar 01 Sell 45.25 3,161 143,035 56,139 03/03/23
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 01 Sell 45.27 1,968 89,091 250,254 03/03/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Mar 01 Sell 45.65 100 4,565 23,048 03/03/23
Huang Dennis Karl See Remarks See Remarks Mar 01 Sell 45.65 389 17,758 75,314 03/03/23
Pinion John Richard See Remarks See Remarks Mar 01 Sell 45.26 3,755 169,951 80,174 03/03/23
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Mar 01 Sell 45.25 3,664 165,796 57,344 03/03/23
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Dec 21 Sell 43.96 2,031 89,283 16,197 12/22/22
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Oct 14 Sell 40.16 1,629 65,421 66,695 10/17/22
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 19 Sell 54.78 295 16,160 36,160 06/22/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Apr 16 Sell 84.55 132 11,161 16,914 04/19/22
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 11 Sell 67.01 10,281 688,930 227,559 03/15/22
Parschauer Karah Herdman EVP and Chief Legal.. EVP and Chief Legal Officer Mar 07 Sell 62.95 5,140 323,563 34,438 03/08/22
Fust Matthew K Director Director Mar 04 Option 40.37 7,500 302,775 23,195 03/08/22
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Mar 01 Sell 65.59 954 62,573 51,808 03/03/22
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Mar 01 Sell 66.62 2,713 180,740 22,317 03/03/22
Pinion John Richard See Remarks See Remarks Mar 01 Sell 66.62 4,498 299,657 45,266 03/03/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Mar 01 Sell 66.62 843 56,161 13,229 03/03/22
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 01 Sell 66.62 2,821 187,935 33,938 03/03/22
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Jan 30 Sell 66.30 1,657 109,859 36,759 02/01/22
Huizenga Theodore Alan SVP, Chief Accountin.. SVP, Chief Accounting Officer Oct 14 Sell 81.14 140 11,360 14,072 10/18/21
Dier Mardi CFO & Executive Vice.. CFO & Executive Vice President Oct 12 Sell 81.98 6,738 552,381 38,762 10/14/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Sep 09 Sell 100.65 7,336 738,368 28,668 09/09/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Sep 09 Option 54.5 7,336 399,812 36,004 09/09/21
Harris Erik EVP & Chief Commerci.. EVP & Chief Commercial Officer Jun 23 Sell 94.8 1,009 95,653 25,708 06/23/21
Kassberg Thomas Richard CBO & EVP CBO & EVP Mar 03 Sell 138.17 4,572 631,713 107,181 03/03/21
Pinion John Richard See Remarks See Remarks Mar 03 Sell 138.17 6,198 856,378 50,237 03/03/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Mar 03 Sell 138.17 3,970 548,535 30,227 03/03/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Mar 03 Sell 138.17 732 101,140 16,544 03/03/21
Bedrosian Camille L EVP and Chief Medica.. EVP and Chief Medical Officer Mar 03 Sell 138.18 4,543 627,752 39,139 03/03/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Jan 08 Option 21 4,000 84,000 20,436 01/08/21
Huizenga Theodore Alan SVP, Controller and.. SVP, Controller and PAO Jan 08 Sell 140.65 4,000 562,600 15,716 01/08/21
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 30 Option 54.5 97 5,286 24,065 10/30/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 30 Sell 100 97 9,700 23,968 10/30/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 13 Option 54.5 10,000 545,000 34,293 10/13/20
Parschauer Karah Herdman EVP and General Coun.. EVP and General Counsel Oct 13 Sell 95 10,000 950,000 24,293 10/13/20